A one-time injection of a novel gene therapy was able to save mice and a newborn calf from succumbing to maple syrup urine ...
A local researcher who is studying treatments for a disease that’s killing citrus trees said her U.S. Department of ...
Scientists have created a new gene therapy for a debilitating genetic disorder called maple syrup urine disease (MSUD). The treatment can prevent recurrence of deadly symptoms in a cow calf born ...
A study by UMass Chan researchers showed that gene therapy correcting the mutation behind maple syrup urine disease (MSUD ... without treatment, has a very similar metabolic profile as the ...
A gene therapy to correct a mutation that causes maple syrup urine disease prevented newborn death and normalized growth in a calf as well as in mice.